Specific Bone Marrow Transplant Treatment Options

The UCSF Benioff Children's Hospital Blood and Marrow Transplant Program offers a variety of specific treatment options for children, including options for those who have:

  • Bone marrow stem cells that are abnormal or defective
  • Cancer that may be cured with a bone marrow transplant
  • A genetic or inherited metabolic disease that affects many organs in the body

These treatment options, called protocols, are all considered research protocols since the patients who participate are treated in a uniform manner and the results, after being collected and evaluated, may be published in a scientific journal. The results of these research protocols are used to advance the use of bone marrow transplantation and allow doctors to develop improved treatment options for all children and adults who may benefit from this type of therapy.

Disease Protocols

At UCSF Benioff Children's Hospital, we offer treatment protocols for various diseases, including:

  • Leukemia, including acute lymphocytic leukemia (ALL), acute myelogenous leukemia (AML)
  • Hodgkins and non-Hodgkins lymphoma
  • Solid tumors including brain tumors and sarcomas
  • High-risk neuroblastoma
  • Severe combined immunodeficiency disease (SCID) and other severe immunodeficiency disorders
  • Genetic diseases, also called metabolic diseases
  • Marrow stem cell defects
  • Hemoglobinopathies

Reducing the Risk of Transplant

Although bone marrow transplant (BMT) remains the best and sometimes only treatment option for some diseases, it does carry certain risks, including damage to healthy tissues such as the brain, lungs, liver and kidneys. While this risk is rather great with a regular BMT, the UCSF Benioff Children's Hospital BMT Program has developed novel protocols to minimize the damage caused by the transplant process with the following:


Reviewed by health care specialists at UCSF Benioff Children's Hospital.

Related Information

UCSF Clinics & Centers

Blood & Marrow Transplant

Blood and Marrow Transplant Program
1975 Fourth St., Sixth Floor
San Francisco, CA 94158
Phone: (415) 476-2188
Fax: (415) 502-4867

Blood & Marrow Transplant Clinic
1825 Fourth St., Sixth Floor
San Francisco, CA 94158
Phone: (415) 353-2986
Fax: (415) 502-4867

Patient Experiences

Our Experts

Morton J. Cowan
Dr. Morton J. Cowan,
pediatric immunologst and bone marrow transplant specialist
Christopher Dvorak
Dr. Christopher Dvorak,
pediatric hematologist and oncologist
Robert E. Goldsby
Dr. Robert E. Goldsby,
pediatric hematologist and oncologist
James Huang
Dr. James Huang,
pediatric hematologist
Lena Winestone
Dr. Lena Winestone,
pediatric hematologist-oncologist