Where I see patients (3)
Biallelic variants of ATP13A3 cause dose-dependent childhood-onset pulmonary arterial hypertension characterised by extreme morbidity and mortality.
Journal of medical genetics
Mortality from Pulmonary Hypertension in the Pediatric Cardiac ICU.
American journal of respiratory and critical care medicine
Safety and Tolerability of a Rapid Transition From Intravenous Treprostinil to Oral Selexipag in Three Adolescent Patients With Pulmonary Arterial Hypertension.
The journal of pediatric pharmacology and therapeutics : JPPT : the official journal of PPAG
A Study to Assess Whether Macitentan Delays Disease Progression in Children With Pulmonary Arte...
Time to the first of the following CEC-confirmed disease progression events: • Death (all causes) • Atrial septostomy or Potts' anastomosis, or registration on lung transplant list • Hospitalization due to worsening PAH • Clinical...
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