Where I see patients (2)
In Utero Enzyme-Replacement Therapy for Infantile-Onset Pompe's Disease.
The New England journal of medicine
The impact of in utero transfusions on perinatal outcomes in patients with alpha thalassemia major: the UCSF registry.
Prenatal Somatic Cell Gene Therapies: Charting a Path Toward Clinical Applications (Proceedings of the CERSI-FDA Meeting).
Journal of clinical pharmacology
Soothing the soul